In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to ...

A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...

Treatment seems to have been effective, but it is not clear whether such bespoke therapies can be widely applied.

An infant with a life-threatening and incurable genetic disease has become the first human to successfully receive a ...

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely ...

LOS ANGELES, May 15 (Xinhua) -- In a groundbreaking medical milestone, U.S. researchers have successfully developed and delivered a personalized gene-editing therapy to treat an infant suffering from ...

Doctors will have to monitor the boy for years to ensure the experimental treatment is effective long-term. But for now, it's ...

researchers led by teams at Children’s Hospital of Philadelphia and University of Pennsylvania report on the first use of the gene-editing technology CRISPR in a customized therapy designed to ...

A baby born with a rare and dangerous genetic disease is thriving after getting an experimental gene editing treatment made ...

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized ...

A new gene therapy developed at the Children's Hospital of Philadelphia has been approved by the FDA and is being used to transform lives. The first patient to receive this gene therapy after it ...