In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to ...

A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...

The process, from diagnosis to treatment, took only six months and marks the first time the technology has been successfully ... Pennsylvania (Penn) developed the customized therapy using the gene ...

G ene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

In a groundbreaking medical milestone, U.S. researchers have successfully developed and delivered a personalized ...

A baby boy with a devastating genetic disease is thriving after becoming the first known person to receive ... these gene and cell therapies,” says Arkasubhra Ghosh, who studies gene therapy ...

An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...

But half of all babies with the disorder die in the first week ... talking about gene editing and the infusions. Doctors applied a personalized treatment to cure a baby’s genetic disorder ...

A baby known as KJ is the first person in the world to receive a customized CRISPR therapy designed to fix a specific ...

Doctors will have to monitor the boy for years to ensure the experimental treatment is effective long-term. But for now, it's ...