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Science Daily3d
Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment
A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...
ExtremeTech on MSN2d
Personalized Gene Therapy Saves Infant With Formerly 'Incurable' Disorder
Doctors will have to monitor the boy for years to ensure the experimental treatment is effective long-term. But for now, it's ...
CBS News20d
First patient to receive gene therapy treatment developed at Children's Hospital of Philadelphia living pain-free
A new gene therapy developed at the Children's Hospital of Philadelphia has been approved by the FDA and is being used to transform lives. The first patient to receive this gene therapy ...
U.S. infant becomes first to receive personalized gene therapy for rare incurable disease
In a groundbreaking medical milestone, U.S. researchers have successfully developed and delivered a personalized gene-editing therapy to treat an infant suffering from a rare and life-threatening ...
The remarkable timeline of a custom gene-editing therapy to save a newborn
News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, ...